Your generous donations will help fast track very promising treatments that will give our precious babies (and so many others like Roman and Stella) a chance at life. Every small donation counts!
WHERE THE MONEY IS GOING:
Contributions will be going to a non-profit foundation that is dedicated to funding research and finding a cure for our children. Their research includes a unique small molecule that passes the blood brain barrier (BBB) and has demonstrated remarkable results at potentially slowing or stopping the rapid course of neurodegeneration that happens in ASMD. Additional research is surrounding a gene therapy that has the potential to replace the defective gene responsible for Roman and Stella's disease with a functioning working copy of the gene for a more permanent treatment.
THERE IS A CLEAR PATH TO TREATMENT:
1. Manufacture clinical grade drug production
2. Final safety studies
3. Get FDA approval to proceed with clinical drug
4. Start clinical trial
If you would like to donate by check directly to the foundation please make it out to --> Wylder Nation Foundation (in memo write #saveromanandstella) and mail to: